#rare-disease
Documents
The potential investment impact of improved access to accelerated approval on the development of treatments for low prevalence rare diseases
Documents
A long diagnostic delay in patients with Hereditary Haemorrhagic Telangiectasia: a questionnaire-based retrospective study
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Key outcomes from stakeholder workshops at a symposium to inform the development of an Australian national plan for rare diseases
Documents
RECOMENDACIONES SOBRE LOS ASPECTOS ÉTICOS DE LOS PROGRAMAS DE CRIBADO DE POBLACIÓN PARAENFERMEDADES RARAS (The Ethicals Aspect s of Population Screening Programme of Rare Diseases)
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